BioMarin Pharmaceutical(BMRN) - 2023 Q4 - Annual Report

BRINEURA is approved for marketing in the U.S. (for ages three and older) and in the EU (for all ages from birth) and in other international markets. ALDURAZYME ALDURAZYME is a highly purified protein that is designed to be identical to a naturally occurring form of the human enzyme alphaL-iduronidase, a lysosomal enzyme normally required for the breakdown of GAGs. MPS I is a progressive and debilitating life-threatening genetic disease that is caused by the deficiency of alpha-L-iduronidase. Patients with ...