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uniQure Announces Positive Interim Data Update Demonstrating Slowing of Disease Progression in Phase I/II Trials of AMT-130 for Huntington's Disease
QUREuniQure(QURE) Newsfilter·2024-07-09 11:05

~ Achieved statistically significant, dose-dependent, and durable evidence of potential therapeutic benefit; Patients receiving high-dose AMT-130 showed 80% slowing of disease progression in the composite Unified Huntington's Disease Rating Scale (cUHDRS) at 24 months compared to a propensity score-weighted external control ~ ~ Investor conference call and webcast today at 8:30 a.m. ET ~ "These updated results are exciting and provide compelling evidence of potential therapeutic benefit," stated Victor Sung ...