– Completed Enrollment of the Phase 3 RISE UP Study of Mitapivat in Sickle Cell Disease; Topline Data from 52-Week Study Expected in Late 2025 – – Received 1.1BillioninPaymentsfromRoyaltyPharmaandServier,FollowingFDAApprovalofVorasidenib––CommencedEnrollmentofthePhase2bStudyofTebapivatinLower−RiskMyelodysplasticSyndromes(LRMDS);GrantedFDAOrphanDrugDesignationforTreatmentofMDS––PYRUKYNDR◯(Mitapivat)NetRevenueof9.0 Million in Q3; Cash, Cash Equivalents and Market ...