The pioneering physician behind groundbreaking ASO therapy

If you can imagine your child seizing all day every day, um, and being having movement disorders, ballistic movement disorders that you can't control, autonomic dysfunction, you know, inability to control breathing, heart rate, I mean, it's just terrible disease. [snorts] And they were there to see if we could help them. And I had to tell them that the indication was just too small for I was to pursue commercially.But in that conversation, I realized that the technology that we had invented was efficient en ...