日本最贵的药3亿497万日元，可走“医保”

Group 1 - The Japanese Ministry of Health, Labour and Welfare has set the price for the gene therapy drug "Elevidys" at 3.497 billion yen (approximately 137.9 million yuan), making it the highest-priced drug in Japan [3] - "Elevidys" is designed for patients suffering from Duchenne muscular dystrophy, which is caused by genetic mutations leading to muscle degeneration and strength loss, and it requires only a single administration for treatment [3] - The decision to approve the drug was made during a meeting of the Central Social Insurance Medical Council, which is an advisory body to the Minister of Health, Labour and Welfare [5] Group 2 - The Japanese Ministry of Health, Labour and Welfare is expected to include "Elevidys" in the national health insurance system on February 20, coinciding with its market launch [5] - The target patient demographic includes children aged 3 to 7 who are able to walk, and testing will be conducted prior to administration to confirm the expected efficacy [5] - The estimated number of eligible patients in Japan for the fiscal year 2026 is projected to be 37, with an expectation of around 20 new cases annually thereafter [5]