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Experimental treatment for rare 'bubble boy disease' could give impacted kids new life
NBC News· 2025-11-18 02:30
This is Elelliana Nakam, a little girl with big dreams. >> I would like to to be an artist. >> Today, the 12-year-old is indoors because she wants to be, not because she has to.The first year of her life was spent in the confines of a sterile environment where doors and windows had to stay shut and visitors had to stay out, all to save her life. At four months old, Elelliana was diagnosed with a rare disease called severe combined immuno deficiency disorder or SKID. Babies born with SKID don't develop the c ...
She was 13 and out of options until an experimental treatment worked #shorts
60 Minutes· 2025-11-12 17:01
It was this tiny little um syringe >> and it was just one injection of this little vial. >> Just one injection of this tiny little vial and that was it. >> Alyssa Tapley, who lives outside London, was diagnosed with a rare form of leukemia.She endured a year of failed treatments, chemotherapy, a bone marrow transplant, and her doctors ran out of options. I was 13 when I was told that I was going to die. >> And they were talking about end of life care.>> Yeah. And I said, "Please don't give up on me because ...