Amicus Therapeutics (FOLD) Presents At MDA Clinical & Scientific Virtual Conference - Slideshow

N-140N-233N-390N-470N-652N-882N-925 rhGAA – kif + Endo H IHC : LC3 II B. 0 1 2 3 4 0 20 40 60 80 100 120 Time (Hours) Normalized GAA Activity(%) Stability in buffer (pH 7.4) 0 1 2 3 4 0 20 40 60 80 100 120 Cipaglucosidase alfa Cipaglucosidase alfa + 17 µM miglustat Cipaglucosidase alfa + 170 µM miglustat Stability in human blood Time (Hours) Normalized GAA Activity(%) Enhancing Delivery of Acid Alpha-Glucosidase (GAA) to Skeletal Muscle in Pompe Disease (PD): Key Challenges and Attributes of AT-GAA Nithya S ...