Scholar Rock Holding (SRRK) presents at 41st Annual J.P. Morgan Healthcare Conference - Slideshow

2/3 of overall patient population Infantile onset; unable to sit up independently © 2022 Scholar Rock, Inc. All rights reserved. Potential to Pioneer a New Treatment Era: Opportunity for Muscle-Directed Therapy to Complement SMN-Directed Therapies alone1, 2, 3,4 *TOPAZ Phase 2 trial evaluated patients with Type 2 and 3 SMA (did not include Type 1) 1. Lally et al, Orphanet Journal of Rare Diseases, 2017; 2. SMA Europe. SMATracker. About SMA. Accessed January 24, 2022. https://smatracker.eu/what-is-spinal-mu ...