Gene therapy candidates for rare diseases

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Solid Biosciences to Participate at the Jefferies Global Healthcare Conference
Globenewswire· 2025-05-28 12:00
Core Insights - Solid Biosciences Inc. is participating in the Jefferies Global Healthcare Conference on June 4, 2025, with a fireside chat featuring the President and CEO, Bo Cumbo, and Chief Medical Officer, Gabriel Brooks [1][2] Company Overview - Solid Biosciences is focused on developing precision genetic medicines targeting rare neuromuscular and cardiac diseases, including Duchenne muscular dystrophy, Friedreich's ataxia, and catecholaminergic polymorphic ventricular tachycardia [3] - The company is advancing a diverse pipeline of gene therapy candidates and innovative libraries of genetic regulators aimed at improving gene therapy delivery across the industry [3] - Solid Biosciences was founded by individuals directly impacted by Duchenne, emphasizing its mission to enhance the daily lives of patients with rare diseases [3]
Solid Biosciences to Participate at The Citizens Life Sciences Conference
Globenewswire· 2025-04-30 12:00
Core Insights - Solid Biosciences Inc. is participating in The Citizens Life Sciences Conference on May 7, 2025, with CEO Bo Cumbo leading a fireside chat [1][2] Company Overview - Solid Biosciences is focused on developing precision genetic medicines targeting rare neuromuscular and cardiac diseases, including Duchenne muscular dystrophy, Friedreich's ataxia, and catecholaminergic polymorphic ventricular tachycardia [3] - The company is advancing a diverse pipeline of gene therapy candidates and innovative technologies aimed at improving gene therapy delivery across the industry [3] - Solid Biosciences was founded by individuals directly impacted by Duchenne, emphasizing its mission to enhance the daily lives of patients with rare diseases [3]