Crysvita (burosumab)

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Assenagon Boosts Ultragenyx Pharmaceutical Inc. (RARE) Stake by 439% Amid Breakthrough Pipeline
Yahoo Financeยท 2025-10-02 13:45
Group 1 - Ultragenyx Pharmaceutical Inc. (NASDAQ:RARE) is recognized as a promising biotech stock, with Assenagon Asset Management increasing its holdings by 439.0% in Q2, acquiring 947,865 shares for a total investment of $42,314,000, representing about 1.23% ownership [1] - The company has received Breakthrough Therapy designation for GTX-102 in Angelman syndrome and is positioned to advance UX143, which is expected to be a transformative treatment for osteogenesis imperfecta in both pediatric and adult patients [2] - Strategic collaborations, including a recent FDA approval for Regeneron's Evkeeza, indicate a positive outlook for Ultragenyx, despite a recent 26% drop in stock price due to a failed treatment approval [3] Group 2 - Ultragenyx is a California-based biopharmaceutical company focused on discovering, developing, and commercializing treatments for rare and ultra-rare genetic diseases, with key products including Crysvita, Mepsevii, Dojolvi, and Evkeeza [4]