| --- | --- | --- | --- | --- | --- | |----------------------------------|-------|-------|-------|-------|-------| | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | | A Global Leader in Gene Therapy | | | | | | | Corporate Presentation | | | | | | | March 2020 | | | | | | uniQure A GLOBAL LEADER IN GENE THERAPY MARCH 2020 | 2 Forward-looking Statements This presentation contains forward-looking statements. All statements other than statements of historical fact are forward- ...

uniQure Delivering Gene Therapy to Patients Corporate Presentation November 2019 D E L I V E R I N G G E N E T H E R A P Y T O P A T I E N T S N O V E M B E R 2 0 1 9 | 2 Forward-looking Statements This presentation contains forward-looking statements. All statements other than statements of historical fact are forward-looking statements, which are often indicated by terms such as "anticipate," "believe," "could," "estimate," "expect," "goal," "intend," "look forward to," "may," "plan," "potential," "predic ...

uniQure Delivering Gene Therapy to Patients Cantor Global Healthcare Conference October 2, 2019 D E L I V E R I N G G E N E T H E R A P Y T O P A T I E N T S S E P T E M B E R 2 0 1 9 | 2 Forward-looking Statements This presentation contains forward-looking statements. All statements other than statements of historical fact are forward-looking statements, which are often indicated by terms such as "anticipate," "believe," "could," "estimate," "expect," "goal," "intend," "look forward to," "may," "plan," "po ...

uniQure Delivering Gene Therapy to Patients Corporate Presentation AULY 2019 DELIVERING GENE THERAPY TO PATIENTS JULY 2019 | 2 Forward-looking Statements This presentation contains forward-looking statements. All statements other than statements of historical fact are forward-looking statements, which are often indicated by terms such as "anticipate," "believe," "could," "estimate," "expect," "goal," "intend," "look forward to," "may," "plan," "potential," "predict," "project," "should," "will," "would" and ...

Towards AAV5-mediated Gene Therapy for Hemophilia A with a Factor IX Variant that functions independently of FVIII Ying Poi Liu1, Vanessa Zancanella1, Betty Au1, Paula Montenegro-Miranda1, Martin de Haan1, Viola J.F. Strijbis2, Mettine H.A. Bos2, Karin Huber3, Joachim Schwäble3, Erhard Seifried3, Pavlina Konstantinova1, Sander Van Deventer1 1uniQure Biopharma B.V., Amsterdam, The Netherlands; 2Div. of Thrombosis and Hemostasis, Einthoven Laboratory for Vascular and Regenerative Medicine, Leiden University M ...

uniQure Sustained mutant huntingtin lowering in Huntington disease minipigs mediated by AAV5-miHTT (AMT-130) gene therapy Astrid Vallès, PhD Senior Scientist, Biomarker Lead - New Therapeutic Target Discovery ASGCT 22nd Annual Meeting - May 1, 2019 Forward-looking Statements This presentation contains forward-looking statements. All statements other than statements of historical fact are forward-looking statements, which are often indicated by terms such as "anticipate," "believe," "could," "estimate," "exp ...

uniQure Delivering Gene Therapy to Patients SVB Leerink March 1, 2019 D E L I V E R I N G G E N E T H E R A P Y T O P A T I E N T S M A R C H 2 0 1 9 | 2 Forward-looking Statements This presentation contains forward-looking statements. All statements other than statements of historical fact are forward-looking statements, which are often indicated by terms such as "anticipate," "believe," "could," "estimate," "expect," "goal," "intend," "look forward to," "may," "plan," "potential," "predict," "project," "s ...